Child Thriving After Becoming World’s Youngest to Receive Gene Therapy for AADC Deficiency

Clinical Trial Success at Cincinnati Children’s Supports Recent US FDA Approval for First Therapy to Directly Replace a Gene in the Brain CINCINNATI, Nov. 15, 2024 /PRNewswire/ — Sriansh Ojha was fully into his “terrible twos” on an April afternoon at Cincinnati Children’s as he squealed…